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Salbutamol increases SMN mRNA and protein levels in spinal muscular atrophy cellsANGELOZZI, C; BORGO, F; TIZIANO, F. D et al.Journal of medical genetics. 2008, Vol 45, Num 1, pp 29-31, issn 0022-2593, 3 p.Article

Randomized, double-blind, placebo-controlled trial of phenylbutyrate in spinal muscular atrophyMERCURI, E; BERTINI, E; CINI, C et al.Neurology. 2007, Vol 68, Num 1, pp 51-55, issn 0028-3878, 5 p.Article

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